How do you approach clinical trial design for cell and gene therapies? There are a lot of similarities, but also some notable differences that I have encountered the last 15 years working in multiple ...
LifeArc partners with Elpida Therapeutics to advance three gene therapies for ultra-rare neurodegenerative diseases in childrenLifeArc provides ...
Authorization advances Fractyl Health to a dual clinical-stage company, with Revita® in pivotal development for post-GLP-1 weight maintenance and ...
UK and US trial sites open; first patient dosed with TGX-007, Trogenix’s proprietary dual-payload AAV gene therapy TGX-007 leverages Trogenix’s precision synthetic super-enhancer platform that ...
Key Points Interested in Opus Genetics, Inc.? Here are five stocks we like better. Opus Genetics highlighted a broad ...
Pancreatitis is a complex inflammatory disease driven by both genetic and environmental factors. It poses substantial ...
Myrtelle, Inc., a clinical-stage gene therapy company selected by the FDA for the START Pilot Program and focused on ...
Regenxbio said its experimental gene therapy for Duchenne muscular dystrophy succeeded in a trial, paving the way for a ...
Venture capitalist Chamath Palihapitiya responded “What?!?!?!” on X, amplifying analyst Cremieux‘s post describing Eli Lilly ...
Four patients with LGMD-R5 (gamma-sarcoglycanopathy, formerly LGMD-2C) have received the ATA-200 gene therapy as part of the ongoing Phase 1b/2 trial evaluating the safety, pharmacodynamics, and ...