The baby saved from a rare disease by a first-ever personalized gene fix has reached a big milestone, taking his first steps ahead of Christmas. KJ Muldoon is walking and getting ready to celebrate ...

A new class of life-saving drugs is helping children who once had no hope. But some carry a price tag of millions for a ...

This year saw notable progress in head and neck cancers, Huntington's disease, personalized genetic therapy, and heart ...

JABSOM Cell and Molecular Biology researcher Dr. Jesse Owens has spent the better part of two decades chasing a vision that ...

Researchers hoped they had finally found a way to get gene therapies past the blood-brain barrier. Then the first patient ...

Vertex Pharmaceuticals presents clinical data demonstrating benefits of Casgevy in SCD and TDT patients aged 5+ at ASH ...

Antibody-based therapies are used to treat numerous diseases, from cancer to rheumatic disorders and multiple sclerosis.

A 10-month-old baby who sparked nationwide headlines after receiving a first-of-its kind gene-editing treatment was released ...

The FDA has issued its stamp of approval to a new, cell-based option to treat Wiskott-Aldrich syndrome (WAS), marking the ...

The treatment uses a modified, harmless virus to deliver healthy genes to a patient’s cells to treat genetic diseases. Read ...

With Strand Life Sciences, Reliance is pushing genetic testing toward the mainstream. Incumbents, regulators and doctors are ...