AUSTIN (KXAN) — An exceptionally rare and fatal genetic disease may finally have a solution. Huntington’s Disease affects one in ten to twenty thousand Americans. The disease is a mixture of dementia ...

UniQure's UQ1.F experimental gene therapy for Huntington's disease slowed progression of the brain disorder by 75% in an early-to-mid stage study, it said on Wednesday. Huntington's is a rare ...

UCL and uniQure report the first treatment to slow Huntington’s disease with gene therapy AMT-130. High-dose patients had 75% less progression over three years compared with standard care. uniQure ...

TAMPA, Fla. (WFLA) — For the first time, scientists have successfully treated someone suffering from Huntington’s disease, a fatal genetic illness with no cure. The Mayo Clinic reports that the ...

A research team says that for the first time in history, it’s successfully treated Huntington’s disease, a devastating and inherited disorder that kills nerve cells and leads to rapid decline and ...

A new discovery offers hope for Huntington’s disease. This discovery provides hope that a DNA repair process may help slow or stop disease progression. Research has identified a critical DNA repair ...

Gene therapy is becoming a powerful way to treat challenging diseases that don’t respond to traditional treatments, and researchers now report the first success in modifying genes to slow Huntington’s ...

Preliminary results from a small trial offer the clearest evidence yet that the brain disease’s progression can be slowed. A one-time gene therapy can markedly slow the progression of Huntington’s ...

An experimental gene therapy was found to slow the progression of Huntington’s disease in a “pivotal” Phase 1/2 study, according to drugmaker uniQure, marking a major step toward a potential first ...

Adam Feuerstein is a senior writer and biotech columnist, reporting on the crossroads of drug development, business, Wall Street, and biotechnology. He is also a co-host of the weekly biotech podcast ...